PTC Acquires Near-Approval ST-920 Fabry Gene Therapy in Bankruptcy Auction

PTC Therapeutics acquires BLA-stage ST-920, a one-time AAV gene therapy for Fabry disease, with potential U.S. launch in 2027 and strong clinical data.

PTC Acquires Near-Approval ST-920 Fabry Gene Therapy in Bankruptcy Auction
Credit: David Paul Morris/Bloomberg
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