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Harmony Biosciences Drug Fails Fragile X Trial: What Went Wrong?

Harmony Biosciences’ experimental drug ZYN002 failed its Phase 3 trial for Fragile X syndrome, failing to meet its main goal for improving social avoidance primarily due to a high placebo response.

Harmony Biosciences Drug Fails Fragile X Trial: What Went Wrong?
Credit: Harmony Biosciences
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09/24/2025 · 9:24 AM
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